Please provide your email address to receive an email when new articles are posted on . Olezarsen lowered triglyceride levels at 6 months in patients with familial chylomicronemia syndrome. The safety ...
Please provide your email address to receive an email when new articles are posted on . The reductions after treatment with evinacumab (Evkeeza, Regeneron) were evident in certain patients from two ...
Lomitapide, in Phase III Development, Holds Orphan Drug Status for Treatment of CAMBRIDGE, Mass., March 15, 2011 (GLOBE NEWSWIRE) -- Aegerion Pharmaceuticals, Inc. (Nasdaq:AEGR), an emerging ...
FDA expands Juxtapid approval for pediatric patients aged 2 years and older with homozygous familial hypercholesterolemia to reduce plasma LDL-C levels.
Credit: Getty Images. In FCS, mutations in the lipoprotein lipase gene lead to an accumulation of chylomicrons in plasma resulting in severe hypertriglyceridemia. Treatment with olezarsen ...
Credit: Ionis Tryngolza is an apoC-III-directed antisense oligonucleotide that is administered subcutaneously once monthly. As an adjunct to a low fat diet, Tryngolza significantly reduced fasting ...
CARLSBAD, Calif., Feb. 15, 2024 /PRNewswire/ -- Ionis Pharmaceuticals (IONS), Inc. (Nasdaq: IONS) announced today that the U.S. Food and Drug Administration (FDA) has granted Orphan Drug designation ...
CARLSBAD, Calif., Dec. 19, 2024 /PRNewswire/ -- Ionis Pharmaceuticals, Inc. (Nasdaq: IONS) announced today that the U.S. Food and Drug Administration (FDA) has approved TRYNGOLZA™ (olezarsen) as an ...
"Our findings suggest that neurodegeneration may underlie pain and cognitive dysfunction in FCS and reinforce the importance of assessing neuropathy in individuals with FCS over time." — Bashir et al.
The AHA has published a scientific statement regarding the screening, diagnosis, and management of hypertriglyceridemia in pediatric patients.
Regeneron’s new med Evkeeza already sports an approval in the ultra-rare disease homozygous familial hypercholesterolemia, which is associated with extreme levels of cholesterol. But thanks to ...
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