Sarepta said DMD treatments Amondys 45 and Vyondys 53 show 'positive and encouraging trends' even though a trial failed to ...

Columnist Betty Vertin shares how she explained Duchenne muscular dystrophy to her sons, who received their DMD diagnosis at a young age.

Dosing has begun in a long-term extension study testing Satellos Bioscience’s experimental oral therapy SAT-3247 in men with ...

Columnist Betty Vertin marks each success with Duchenne MD with the refrain, "Not today, Duchenne," but she dreads when "today" will come.

As columnist Robin Stemple's FSHD progresses, he worries about how his increased care needs will affect his family caregivers ...

In a $12 billion deal, Novartis has agreed to acquire Avidity Biosciences, which is developing several treatments for ...

Bridgebio Pharma says it will seek U.S. approval of BBP-418 for LGMD2i after Phase 3 trial data showed a range of benefits ...

Learn how Duchenne muscular dystrophy affects oral health and explore tips for daily care, dental visits, and preventing ...

Learning how to talk to doctors about Duchenne muscular dystrophy can help support you in your role as a caregiver for ...

Columnist Betty Vertin doesn't often dwell on her caregiver grief, but sometimes she needs to embrace it and let it flow through her.

Use of the oral therapy BBP-418 appeared to improve walking ability and lung function in people with limb-girdle muscular dystrophy type 2i (LGMD2i) — characterized by muscle wasting at the shoulders ...

Living with muscular dystrophy can be challenging, and there are considerations that must be taken into account on a day-to-basis and in certain situations to help patients manage the disease. Many ...