There’s a moment from junior high seared into my memory, when another kid asked me why I had “all those red bumps on my arms.” It was something that until then I had barely noticed; after his comment, ...

DelveInsight’s, “Urea Cycle Disorders - Pipeline Insight, 2025,” report provides comprehensive insights about 8+ companies and 8+ pipeline drugs in Urea Cycle Disorders pipeline landscape. It covers ...

New York, USA, June 19, 2025 (GLOBE NEWSWIRE) -- Urea Cycle Disorders Market to Register Sustainable Growth During the Study Period (2020–2034) | DelveInsight According to DelveInsight’s analysis, the ...

The National Urea Cycle Disorders Foundation (NUCDF), the leading patient advocacy group for people affected by urea cycle disorders (UCDs), today announced the launch of a two-year national project ...

Two infusions of a customized CRISPR base-editing therapy showed benefit in a baby with an ultra-rare inborn error of metabolism affecting the urea cycle. Once ...

The rare genetic disease kills 50% of babies diagnosed with it by early infancy. Just six months after a newborn at Children's Hospital of Philadelphia was diagnosed with a rare and life-threatening ...

Preclinical data to showcase the potential of regRNA-targeting to increase protein levels in a clinically meaningful way by upregulating gene expression Interim safety data including patient ...

An Indiana University School of Medicine physician scientist is making strides in understanding the molecular origins of fatty liver disease, a leading cause of liver failure in the United States. By ...

Urea cycle disorders (UCDs) are a group of diseases. They make it hard for your child’s body to remove waste products as they digest proteins. They are inherited diseases -- you pass them down to your ...

Brooklyn, New York, Feb. 27, 2023 (GLOBE NEWSWIRE) -- According to a new market research report published by Global Market Estimates, the Global Urea Cycle Disorder Market is estimated to be valued at ...